{"id":3853,"date":"2025-05-15T23:02:32","date_gmt":"2025-05-15T23:02:32","guid":{"rendered":"https:\/\/mailitics.com\/index.php\/2025\/05\/15\/asgct-crispr-personalized-genome-editing-baby\/"},"modified":"2025-05-15T23:02:32","modified_gmt":"2025-05-15T23:02:32","slug":"asgct-crispr-personalized-genome-editing-baby","status":"publish","type":"post","link":"https:\/\/mailitics.com\/index.php\/2025\/05\/15\/asgct-crispr-personalized-genome-editing-baby\/","title":{"rendered":"STAT+: Day 2 of ASGCT: Good news for Baby KJ and the dream of personalized gene editing"},"content":{"rendered":"

STAT+: Day 2 of ASGCT: Good news for Baby KJ and the dream of personalized gene editing
\n \t

\n
<\/BR>
\n
\n \t

\n
<\/BR><\/p>\n

\n

NEW ORLEANS \u2014 Greetings from ASGCT, where the gene therapy\u00a0field had some great news for once, about a highly\u00a0photogenic infant.\u00a0<\/p>\n

Baby KJ gets a custom CRISPR edit to his genome<\/h2>\n

Kiran Musunuru, a researcher at the University of Pennsylvania, announced on stage Thursday that he and collaborators had, for the first time, reached into the genome of a severely ill child and rewritten the unique misspelling in his DNA.<\/p>\n

The custom CRISPR treatment, built for just a single infant named KJ, was a landmark in the 50-year quest to read and repair the code of life. Musunuru and his collaborators, along with outside researchers and advocates, hope they\u2019ve provided a blueprint for treating other children and adults facing deadly diseases caused by unique or ultra-rare mutations.<\/p>\n

Continue to STAT+ to read the full story\u2026<\/a><\/p>\n<\/div>\n

\t

\n
<\/BR>
\n Jason Mast
\n \t

\n
<\/BR>
\nGo to statnews<\/a>
\n \t

\n
<\/BR><\/p>\n","protected":false},"excerpt":{"rendered":"

STAT+: Day 2 of ASGCT: Good news for Baby KJ and the dream of personalized gene editing NEW ORLEANS \u2014 Greetings from ASGCT, where the gene therapy\u00a0field had some great news for once, about a highly\u00a0photogenic infant.\u00a0 Baby KJ gets a custom CRISPR edit to his genome Kiran Musunuru, a researcher at the University of […]<\/p>\n","protected":false},"author":2,"featured_media":0,"comment_status":"closed","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[2194,2658,2679,1428,2218,2678,858,2152],"tags":[2150],"class_list":["post-3853","post","type-post","status-publish","format-standard","hentry","category-biotech","category-crispr","category-gene-editing","category-health","category-in-the-lab","category-rare-diseases","category-research","category-stat","tag-statnews"],"_links":{"self":[{"href":"https:\/\/mailitics.com\/index.php\/wp-json\/wp\/v2\/posts\/3853"}],"collection":[{"href":"https:\/\/mailitics.com\/index.php\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/mailitics.com\/index.php\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/mailitics.com\/index.php\/wp-json\/wp\/v2\/users\/2"}],"replies":[{"embeddable":true,"href":"https:\/\/mailitics.com\/index.php\/wp-json\/wp\/v2\/comments?post=3853"}],"version-history":[{"count":0,"href":"https:\/\/mailitics.com\/index.php\/wp-json\/wp\/v2\/posts\/3853\/revisions"}],"wp:attachment":[{"href":"https:\/\/mailitics.com\/index.php\/wp-json\/wp\/v2\/media?parent=3853"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/mailitics.com\/index.php\/wp-json\/wp\/v2\/categories?post=3853"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/mailitics.com\/index.php\/wp-json\/wp\/v2\/tags?post=3853"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}